Persistent growth-promoting effects of vosoritide in children with achondroplasia are accompanied by improvements in physical and social aspects of health-related quality of life – GENETICS IN MEDICINE

Savarirayan, R; Irving, M; Wilcox, WR; Bacino, CA; Hoover-Fong, JE; Harmatz, P; Polgreen, LE; Mohnike, K; Prada, CE; Kubota, T; Arundel, P; Leiva-Gea, A; Rowell, R; Low, A; Sabir, I; Huntsman-Labed, A; Day, J – 2024 – 10.1016/j.gim.2024.101274