Once-daily, subcutaneous vosoritide therapy in children with achondroplasia: a randomised, double-blind, phase 3, placebo-controlled, multicentre trial

Savarirayan, R; Tofts, L; Irving, M; Wilcox, W; Bacino, CA; Hoover-Fong, J; Font, RU; Harmatz, P; Rutsch, F; Bober, MB; Polgreen, LE; Ginebreda, I; Mohnike, K; Charrow, J; Hoernschemeyer, D; Ozono, K; Alanay, Y; Arundel, P; Kagami, S; Yasui, N; White, KK; Saal, HM; Leiva-Gea, A; Luna-Gonzalez, F; Mochizuki, H; Basel, D; Porco, DM; Jayaram, K; Fisheleva, E; Huntsman-Labed, A; Day, J – 2020